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Everolimus for cardiac rhabdomyomas in children with tuberous sclerosis. The ORACLE study protocol (everOlimus for caRdiac rhAbdomyomas in tuberous sCLErosis): a randomised, multicentre, placebo-controlled, double-blind phase II trial.
Stelmaszewski, Erica V; Parente, Daniella B; Farina, Alberto; Stein, Anna; Gutierrez, Anthony; Raquelo-Menegassio, Antonio F; Manterola, Carla; de Sousa, Carolina F; Victor, Carolina; Maki, Dina; Morón, Elias M; de Abrantes, Fabiano F; Iqbal, Fatima; Camacho-Vilchez, Jazmin; Jimenez-Pavón, Joanna; Polania, Juan P; Thompson, Lorenzo; Bonanato, Lygia; Diebold, Matthias; Da Silva, Maria V C P; Nashwan, Mariam W J; Galvani, Marianna A G; Idris, Osama E A; Danos, Pierina; Ortiz-Lopez, Rocio; Mahmoud, Rofida A A; Gresse, Sergio; Loss, Karla L.
Afiliação
  • Stelmaszewski EV; Pediatric Cardiology Department, Hospital de Pediatría Garrahan, Buenos Aires, Argentina.
  • Parente DB; Radiology Department, D'Or Institute for Research and Education, Federal University of Rio de Janeiro, Rio de Janeiro, Brazil.
  • Farina A; Medical Affairs Department, Mundipharma Pharmaceuticals SRL, Milan, Italy.
  • Stein A; Nephrology Department, Hospital Moinhos de Vento, Porto Alegre, Brazil.
  • Gutierrez A; Medical Department, Pontificia Universidad Católica Madre y Maestra, Facultad Ciencias de la Salud, Santiago de los Caballeros, Dominican Republic.
  • Raquelo-Menegassio AF; Medical Department, Escola Bahiana de Medicina e Saúde Pública, Salvador, Bahía, Brazil.
  • Manterola C; Neurology Department, Clínica Alemana de Santiago/Facultad de Medicina, Universidad de Chile, Santiago, Chile.
  • de Sousa CF; Pharmacy Department, Faculdades Oswaldo Cruz, São Paulo, Brazil.
  • Victor C; Oncology Department, Instituto do Cáncer do Estado de São Paulo (ICESP), São Paulo, Brazil.
  • Maki D; Nephrology Department, Hamad General Hospital, Hamad Medical Corporation (HMC), Doha, Qatar.
  • Morón EM; Adjunct Faculty, Community and Public Health Sciences Department, Nova Southeastern University College of Dental Medicine, Davie, FL, USA.
  • de Abrantes FF; Community Dentistry and Behavioral Science Department, University of Florida College of Dentistry, Gainesville, FL, USA.
  • Iqbal F; Neurology Department, Universidade Federal da São Paulo (UNIFESP), São Paulo, Brazil.
  • Camacho-Vilchez J; Infectious Diseases Department, Communicable Disease Center, Doha, Qatar.
  • Jimenez-Pavón J; Oncology Department, Instituto Nacional del Cancer "Rosa Emilia Sanchez Perez de Tavares" C/Correa y Cidrón, Ciudad Universitaria, Santo Domingo, Dominican Republic.
  • Polania JP; Mood Disorders Department, National Institute of Psychiatry, México City, México.
  • Thompson L; Pediatric Neurology Department, Hospital Pediatrico la Misericordia, Bogotá, Colombia.
  • Bonanato L; Medical Department, Universidad Iberoamericana Unibe, Santo Domingo, Dominican Republic.
  • Diebold M; Medical Department, Eurofarma, São Paulo, Brazil.
  • Da Silva MVCP; Nephrology Department, Cardiovascular Research Institute, Basel, Switzerland.
  • Nashwan MWJ; Ophthalmology Department, Princess Margaret Cancer Center, University of Toronto, Toronto, Ontario, Canada.
  • Galvani MAG; Medical Department, University of Jordan, Amman, Jordan.
  • Idris OEA; Emergency Department, Hamad Medical Corporation, Doha, Qatar.
  • Danos P; Oncology Department, Faculdade de Medicina do ABC, Santo André, Brazil.
  • Ortiz-Lopez R; Geriatric Department, Hamad General Hospital, Hamad Medical Corporation, Doha, Qatar.
  • Mahmoud RAA; Genetics and Molecular Biology Department, Centro de Genética y Biología Molecular (CGBM), Instituto de Investigación - Facultad de Medicina Humana, Universidad de San Martín de Porres (USMP), La Molina, Lima, Perú.
  • Gresse S; Medical Department, Escuela de Medicina y Ciencias de la Salud, Tecnologico de Monterrey, Monterrey, Mexico.
  • Loss KL; Pharmacy Department, Hamad Medical Corporation, Doha, Qatar.
Cardiol Young ; 30(3): 337-345, 2020 Mar.
Article em En | MEDLINE | ID: mdl-31983379

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Rabdomioma / Esclerose Tuberosa / Everolimo / Neoplasias Cardíacas / Antineoplásicos Tipo de estudo: Clinical_trials / Guideline / Observational_studies / Risk_factors_studies Aspecto: Patient_preference Limite: Child / Humans Idioma: En Revista: Cardiol Young Assunto da revista: ANGIOLOGIA / CARDIOLOGIA / PEDIATRIA Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Argentina País de publicação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Rabdomioma / Esclerose Tuberosa / Everolimo / Neoplasias Cardíacas / Antineoplásicos Tipo de estudo: Clinical_trials / Guideline / Observational_studies / Risk_factors_studies Aspecto: Patient_preference Limite: Child / Humans Idioma: En Revista: Cardiol Young Assunto da revista: ANGIOLOGIA / CARDIOLOGIA / PEDIATRIA Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Argentina País de publicação: Reino Unido