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Paediatric patients with heterozygous familial hypercholesterolaemia treated with evolocumab for 80 weeks (HAUSER-OLE): a single-arm, multicentre, open-label extension of HAUSER-RCT.
Santos, Raul D; Ruzza, Andrea; Hovingh, G Kees; Stefanutti, Claudia; Mach, François; Descamps, Olivier S; Bergeron, Jean; Wang, Bei; Bartuli, Andrea; Buonuomo, Paola Sabrina; Greber-Platzer, Susanne; Luirink, Ilse; Bhatia, Ajay K; Raal, Frederick J; Kastelein, John J P; Wiegman, Albert; Gaudet, Daniel.
Afiliação
  • Santos RD; Lipid Clinic Heart Institute, University of São Paulo Medical School Hospital and Hospital Israelita Albert Einstein, São Paulo, Brazil.
  • Ruzza A; Global Clinical Development, Amgen, Thousand Oaks, CA, USA.
  • Hovingh GK; Department of Vascular Medicine, Amsterdam University Medical Center, Amsterdam, Netherlands.
  • Stefanutti C; Department of Molecular Medicine, Umberto I Hospital, Sapienza University of Rome, Rome, Italy.
  • Mach F; Cardiology Department, Geneva University Hospitals, Geneva, Switzerland.
  • Descamps OS; Department of Internal Medicine, Pole Hospitalier Jolimont, Reseau HELORA, La Louviere, Belgium.
  • Bergeron J; Department of Medicine, Centre Hospitalier Universitaire de Québec-Université Laval, Québec, QC, Canada.
  • Wang B; Biostatistics Department, Amgen, Thousand Oaks, CA, USA.
  • Bartuli A; Rare Diseases and Medical Genetics Unit, Bambino Gesù Children's Hospital IRCCS, Rome, Italy.
  • Buonuomo PS; Rare Diseases and Medical Genetics Unit, Bambino Gesù Children's Hospital IRCCS, Rome, Italy.
  • Greber-Platzer S; Division of Pediatric Pulmonology, Allergology and Endocrinology, Department of Pediatrics and Adolescent Medicine, Medical University of Vienna, Vienna, Austria.
  • Luirink I; Department of Paediatrics, Amsterdam University Medical Center, Amsterdam, Netherlands.
  • Bhatia AK; Global Clinical Development, Amgen, Thousand Oaks, CA, USA.
  • Raal FJ; Faculty of Health Sciences, University of the Witwatersrand, Johannesburg, South Africa.
  • Kastelein JJP; Department of Vascular Medicine, Amsterdam University Medical Center, Amsterdam, Netherlands.
  • Wiegman A; Department of Paediatrics, Amsterdam University Medical Center, Amsterdam, Netherlands.
  • Gaudet D; Clinical Lipidology and Rare Lipid Disorders Unit, Community Genomic Medicine Centre and Department of Medicine and ECOGENE-21, Université de Montreal, Chicoutimi, Québec, QC, Canada. Electronic address: daniel.gaudet@umontreal.ca.
Lancet Diabetes Endocrinol ; 10(10): 732-740, 2022 10.
Article em En | MEDLINE | ID: mdl-36075246

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Inibidores de Hidroximetilglutaril-CoA Redutases / Hiperlipoproteinemia Tipo II / Anticolesterolemiantes Tipo de estudo: Clinical_trials Limite: Child / Humans Idioma: En Revista: Lancet Diabetes Endocrinol Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Brasil País de publicação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Inibidores de Hidroximetilglutaril-CoA Redutases / Hiperlipoproteinemia Tipo II / Anticolesterolemiantes Tipo de estudo: Clinical_trials Limite: Child / Humans Idioma: En Revista: Lancet Diabetes Endocrinol Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Brasil País de publicação: Reino Unido